Dr. Tippi MacKenzie (left) of UCSF Benioff Children’s Hospital San Francisco, visits with newborn Elianna and parents Nichelle Obar and Chris Constantino. Photo by Noah Berger Alpha thalassemia major is, by any stretch of the imagination, a dreadful, heart breaker of a disease. It's caused by four missing or mutated genes and it almost always … Continue reading Surviving with Joy
Dr. Tippi MacKenzie
Stem cell transplant in utero offers potential treatment for congenital diseases
Dr. Tippi Mackenzie, UCSFImage Credit: UCSF Each year, around 24,000 women in the US lose a pregnancy. One reason for this unfortunate occurrence are metabolic disorders, one of which is known as Sly syndrome and is caused by a single genetic mutation. In Sly syndrome, the body's cells lack an enzyme necessary for proper cell … Continue reading Stem cell transplant in utero offers potential treatment for congenital diseases
Performance, Passion and Progress: and that’s just page one of our 2018 Annual Report
It’s hard to sum up the activities and achievements of a year in a single document, let alone one that’s just 24 pages. But that’s what we have done in putting together our 2018 Annual Report. It’s a look back at the year just gone, the highlights, the low lights (spoiler alert – there weren’t … Continue reading Performance, Passion and Progress: and that’s just page one of our 2018 Annual Report
CIRM funded study results in the first ever in utero stem cell transplant to treat alpha thalassemia
Imagine being able to cure a genetic disorder before a baby is even born. Thanks to a CIRM funded study, what would have been a mere dream a couple of years ago has become a reality. Drs. Tippi MacKenzie and Juan Gonzalez Velez of the University of California San Francisco (UCSF) have successfully treated alpha … Continue reading CIRM funded study results in the first ever in utero stem cell transplant to treat alpha thalassemia
The Stem Cellar 