Jordan Janz knows how lucky he is. It's been almost six years since Jordan volunteered to be patient number one in a clinical trial at the University of California, San Diego (UCSD) to test a new treatment for cystinosis. People with this rare genetic disease accumulate the amino acid cystine in their organs. The toxic … Continue reading A treatment for one rare disease but plans for many more
Events
Winner of Beast Games becomes champion for his son’s rare disease
You can do a lot with $10 million. Yet, when Jeffrey Randall Allen won the largest prize in game show history on Amazon Prime Video’s Beast Games there was only one thing he wanted to spend his $10 million on—research that might help find a cure for his son’s rare disease. “When my youngest son, … Continue reading Winner of Beast Games becomes champion for his son’s rare disease
The evolution of a CIRM-funded therapy for macular degeneration
Image Credit: University of Southern California (USC) Eye Institute Over the last two decades CIRM has supported research and helped advance potential treatments for macular degeneration, one of the leading causes of blindness. Early grants One of the earliest was a 2007 SEED grant to David Hinton, MD, of the University of Southern California (USC). … Continue reading The evolution of a CIRM-funded therapy for macular degeneration
World AIDS Day at the 3rd Annual Timothy Ray Brown Community Cure Symposium
Event recap written by guest writer Jacqueline Hantgan, CIRM Sr. Outreach Advisor for Outreach and Advocacy December is HIV/AIDS Awareness Month. To commemorate this important event, CIRM recently supported the 3rd Annual Timothy Ray Brown Community Cure Symposium which took place at the Palm Springs Art Museum on World AIDS Day−December 1, 2024. It was … Continue reading World AIDS Day at the 3rd Annual Timothy Ray Brown Community Cure Symposium
California advancing our understanding of Alzheimer’s disease using stem cells
More than 14,000 people in Fresno County live with Alzheimer’s, and an estimated 720,000 Californians face the disease statewide. That’s why the California Institute for Regenerative Medicine (CIRM)—the state agency funding regenerative medicine research—joined the Alzheimer’s Association Walk to End Alzheimer’s in Fresno/Madera to highlight the cell and gene therapy research we support. More than … Continue reading California advancing our understanding of Alzheimer’s disease using stem cells
Next Generation of Regenerative Medicine Scientists and the Golden Era of Biomedical Innovation
CIRM CEO and President, Jonathan 'JT' Thomas speaking in front of conference attendees. During the first-ever California Institute for Regenerative Medicine (CIRM) Trainee Networking Conference, more than 400 students and postdoctoral fellows from CIRM's Bridges, COMPASS, and Scholars programs gathered from different parts of California for a three-day event at the University of Southern California … Continue reading Next Generation of Regenerative Medicine Scientists and the Golden Era of Biomedical Innovation
Exploring Advances in Eye Disease Webinar
The California Institute for Regenerative Medicine (CIRM) has been at the forefront of advancing cellular and gene therapies for various forms of vision loss—including retinitis pigmentosa (RP)—making significant progress in this critical field. Ongoing research and clinical trials are vital to further these advancements. We invite you to join our webinar, Exploring Advances in Eye Disease … Continue reading Exploring Advances in Eye Disease Webinar
Bringing a community together at the 2nd Annual ALSP Conference
In addition to funding innovative programs and research that accelerate the development of stem cell and gene therapy treatments, the California Institute for Regenerative Medicine (CIRM) provides funding to support valuable mission-specific scientific conferences where people can meet to exchange scientific information to meet goals relevant to CIRM’s mission. Recently, CIRM supported the 2nd Annual … Continue reading Bringing a community together at the 2nd Annual ALSP Conference
How CIRM’s high school internship program inspired this scientist’s career path
Photos courtesy of Rashi Ranjan Each year, interns and trainees from the California Institute for Regenerative Medicine (CIRM) education and training programs celebrate achievements, whether that’s making new discoveries in their cell and gene therapy research or advancing to the next phase of their professional journey. This summer, Rashi Ranjan—a former SPARK high school intern—is … Continue reading How CIRM’s high school internship program inspired this scientist’s career path
How CIRM is moving to raise awareness of Parkinson’s Disease
Crissy Field was filled with vibrant colors and massive energy for the 10th annual Moving Day San Francisco event on Saturday, May 4th. Even with the rain and wind, community members showed up to demonstrate their commitment to "moving to end Parkinson's." Moving Day is an annual fundraising walk that unites people living with Parkinson’s Disease, their caregivers, and … Continue reading How CIRM is moving to raise awareness of Parkinson’s Disease