Jordan Janz knows how lucky he is. It's been almost six years since Jordan volunteered to be patient number one in a clinical trial at the University of California, San Diego (UCSD) to test a new treatment for cystinosis. People with this rare genetic disease accumulate the amino acid cystine in their organs. The toxic … Continue reading Treatment for one rare disease but plans for many more
Events
The California Institute for Regenerative Medicine (CIRM) regularly participates in public events across the state to help share details of how the agency supports research, clinical trials, educational programs, and infrastructure that help further the creation of new gene and cell therapies to treat disease.
Winner of Beast Games becomes champion for his son’s rare disease
You can do a lot with $10 million. Yet when Jeffrey Randall Allen won the largest prize in Amazon Prime Video’s Beast Games, he wanted to use it for one purpose: supporting research that might help cure his son’s rare disease. “When my youngest son, Lucas, turned eight months old, we noticed he was missing … Continue reading Winner of Beast Games becomes champion for his son’s rare disease
California advancing our understanding of Alzheimer’s disease using stem cells
More than 14,000 people in Fresno County live with Alzheimer’s, and an estimated 720,000 Californians face the disease statewide. That’s why the California Institute for Regenerative Medicine (CIRM)—the state agency funding regenerative medicine research—joined the Alzheimer’s Association Walk to End Alzheimer’s in Fresno/Madera to highlight the cell and gene therapy research we support. More than … Continue reading California advancing our understanding of Alzheimer’s disease using stem cells
Bringing a community together at the 2nd Annual ALSP Conference
In addition to funding programs that advance stem cell and gene therapy development, CIRM supports mission‑focused scientific conferences that foster information exchange aligned with its goals. Second annual ALSP Conference Recently, CIRM supported the 2nd Annual ALSP Community Conference: Insights and Potential of Cell‑Based Therapies for Leukodystrophies. The conference brought together patients, advocates, care partners, … Continue reading Bringing a community together at the 2nd Annual ALSP Conference
Raising awareness of Parkinson’s Disease
Crissy Field was filled with vibrant colors and massive energy for the 10th annual Moving Day San Francisco event on Saturday, May 4th. Even with the rain and wind, community members showed up to demonstrate their commitment to "moving to end Parkinson's." Moving Day is an annual fundraising walk that brings together people with Parkinson’s disease, … Continue reading Raising awareness of Parkinson’s Disease
CIRM team shines at ASGCT annual meeting in sunny Los Angeles
The California Institute for Regenerative Medicine (CIRM) team spent a week in sunny Los Angeles spreading awareness of its mission at the American Society of Gene & Cell Therapy (ASGCT) annual meeting. The meeting provides a place for people in the cell and gene therapy field to learn from the latest scientific research, stay up … Continue reading CIRM team shines at ASGCT annual meeting in sunny Los Angeles
A Month of CIRM: Where we’ve been, where we’re going
All this month we are using our blog and social media to highlight a new chapter in CIRM’s life, thanks to the voters approving Proposition 14. We are looking back at what we have done since we were created in 2004, and also looking forward to the future. We kick off this event with a … Continue reading A Month of CIRM: Where we’ve been, where we’re going
It’s official: the state of regenerative medicine is strong
A panel discussion to a packed house at the annual ARM State of the Industry briefing Calling it a “year of dramatic impact for patients” Janet Lambert, the CEO of the Alliance for Regenerative Medicine (ARM), gave the annual “State of the Industry” briefing today in San Francisco. The briefing is a traditional kick-off event … Continue reading It’s official: the state of regenerative medicine is strong
Tips on how to be a great Patient Advocate from three of the best Advocates around
No one sets out to be a Patient Advocate. It’s something that you become because of something that happens to you. Usually it’s because you, or a loved one or a friend, becomes ill and you want to help find a treatment. Whatever the reason, it is the start of a journey that often throws … Continue reading Tips on how to be a great Patient Advocate from three of the best Advocates around
Join us for our next installment of “Ask The Experts” on July 31st.
Join us for our second installment of “Ask the Expert” at 12pm, PST on July 31st! This live interactive event will feature a conversation between Drs. Clive Svendsen, Robert Baloh from Cedars-Sinai, Dr. Ralph Kern, the Chief Operating Officer and Chief Medical Officer of Brainstorm Therapeutics, and CIRM Senior Science Officer Dr. Lila Collins. In … Continue reading Join us for our next installment of “Ask The Experts” on July 31st.