Tomorrow, February 28th, is Rare Disease Day. It’s a day to remind ourselves of the millions of people, and their families, struggling with these diseases. These conditions are also called orphan diseases because, in many cases, drug companies were not interested in adopting them to develop treatments. Here at the California Institute for Regenerative Medicine (CIRM), we … Continue reading Join the movement to fight rare diseases
National Institutes of Health
Reasons to be thankful this Thanksgiving: creative nerds
We at the California Institute for Regenerative Medicine have a lot to be thankful for this Thanksgiving. We get to work with some extraordinary colleagues, we get to know some remarkable patient advocates who are pioneers in volunteering for stem cell and gene therapies, and we have a front row seat in a movement that … Continue reading Reasons to be thankful this Thanksgiving: creative nerds
From our house to the White House. Kinda
Jackie Ward, PhD. Photo courtesy National Institute of Neurological Diseases and Stroke It's always fun to meet someone early in their career and see how they grow and evolve and take on new challenges. I first met Jackie Ward when she received a training grant from CIRM while she studied for her PhD at the … Continue reading From our house to the White House. Kinda
CIRM Board gives thumbs up to training and treatment programs
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST CIRM Bridges student discusses her poster presentation At CIRM, the bread and butter of what we do is funding research and hopefully advancing therapies to patients. But the jam, that's our education programs. Helping train the next generation of stem cell and gene therapy scientists is … Continue reading CIRM Board gives thumbs up to training and treatment programs
Building a better brain (model) in the lab
Leica Picture of a brain organoid: courtesy National Institute of Allergy and Infectious Diseases, NIH One of the biggest problems with trying to understand what is happening in a disease that affects the brain is that it’s really difficult to see what is going on inside someone’s head. People tend to object to you trying … Continue reading Building a better brain (model) in the lab
CIRM new hires include a few former employees
CIRM new hires include former employees and some new faces, all focused on the agency's mission. Rosa Canet-Aviles, PhD Rosa has been named the new Vice President of Scientific Programs. Rosa is a familiar face at the agency, serving as a Science Officer with CIRM from 2008 to 2014. During that time, she helped oversee … Continue reading CIRM new hires include a few former employees
Call for a worldwide approach to regulating predatory stem cell clinics
You can’t fix a global problem at the local level. That’s the gist of a new perspective piece in the journal Stem Cell Reports that calls for a global approach to rogue stem cell clinics that offer bogus therapies. The authors of the article are calling on the World Health Organization (WHO) to set up … Continue reading Call for a worldwide approach to regulating predatory stem cell clinics
Regulated, Reputable and Reliable: FDA’s Taking Additional Steps to Advance Safe and Effective Regenerative Medicine Products
Peter Marks, M.D., Ph.D., Director, Center for Biologics Evaluation and Research In February 2020, CIRM presented a series of benchmarks for the responsible delivery of stem cell and regenerative medicine products. These benchmarks are outlined in the publication Regulated, reliable and reputable: Protect patients with uniform standards for stem cell treatments. In a nutshell, CIRM … Continue reading Regulated, Reputable and Reliable: FDA’s Taking Additional Steps to Advance Safe and Effective Regenerative Medicine Products
Three UC’s Join Forces to Launch CRISPR Clinical Trial Targeting Sickle Cell Disease
Sickle shaped red blood cells The University of California, San Francisco (UCSF), in collaboration with UC Berkeley (UCB) and UC Los Angeles (UCLA), have been given permission by the US Food and Drug Administration (FDA) to launch a first-in-human clinical trial using CRISPR technology as a gene-editing technique to cure Sickle Cell Disease. This research … Continue reading Three UC’s Join Forces to Launch CRISPR Clinical Trial Targeting Sickle Cell Disease
Hitting our goals: regulatory reform
Way, way back in 2015 – seems like a lifetime ago doesn’t it – the team at CIRM sat down and planned out our Big 6 goals for the next five years. The end result was a Strategic Plan that was bold, ambitious and set us on course to do great things or kill ourselves … Continue reading Hitting our goals: regulatory reform