How can something that affects 30 million Americans, one in ten people in the US, be called rare? But that’s the case with people who have a rare disease. There are around 7,000 different diseases that are categorized as rare because they affect fewer than 200,000 people. Less than five percent of these diseases have … Continue reading Breaking the isolation of rare diseases
Clinical Trials
Friday Roundup: A better kind of blood stem cell transplant; Encouraging news from spinal cord injury trial; Finding an “elusive” cell that could help diabetics
Cool Instagram image of the week: Chemo- and radiation-free blood stem cell transplant showing promise Bubble baby disease, also known as severe combined immunodeficiency (SCID), is an inherited disorder that leaves newborns without an effective immune system. Currently, the only approved treatment for SCID is a blood stem cell transplant, in which the patient’s defective … Continue reading Friday Roundup: A better kind of blood stem cell transplant; Encouraging news from spinal cord injury trial; Finding an “elusive” cell that could help diabetics
Stem Cell Agency invests in stem cell therapies targeting sickle cell disease and solid cancers
Today CIRM’s governing Board invested almost $10 million in stem cell research for sickle cell disease and patients with solid cancer tumors. Clinical trial for sickle cell disease City of Hope was awarded $5.74 million to launch a Phase 1 clinical trial testing a stem cell-based therapy for adult patients with severe sickle cell disease … Continue reading Stem Cell Agency invests in stem cell therapies targeting sickle cell disease and solid cancers
A Noble pursuit; finding the best science to help the most people
Mark Noble, Ph.D., is a pioneer in stem cell research and the Director of the University of Rochester Stem Cell and Regenerative Medicine Institute in New York. He is also a member of CIRM’s Grants Working Group (GWG), the panel of independent scientific experts we use to review research applications for funding and decide which … Continue reading A Noble pursuit; finding the best science to help the most people
Seeing is believing. Proof a CIRM-funded therapy is making a difference
You have almost certainly never heard of Thelma, or met her, or know anything about her. She’s a lady living in England who, if it wasn’t for a CIRM-funded therapy, might not be living at all. She’s proof that what we do, is helping people. Thelma is featured in a video about a treatment for … Continue reading Seeing is believing. Proof a CIRM-funded therapy is making a difference
California gets first royalty check from Stem Cell Agency investments
CIRM recently shared in a little piece of history. The first royalty check, based on CIRM’s investment in stem cell research, was sent to the California State Treasurer’s office from City of Hope. It’s the first of what we hope will be many such checks, helping repay, not just the investment the state made in … Continue reading California gets first royalty check from Stem Cell Agency investments
Just a Mom: The Journey of a Sickle Cell Disease Patient Advocate [video]
Adrienne Shapiro will tell you that she’s just a mom. And it’s true. She is just a mom. Just a mom who is the fourth generation of mothers in her family to have children born with sickle cell disease. Just a mom who was an early advocate of innovative stem cell and gene therapy research … Continue reading Just a Mom: The Journey of a Sickle Cell Disease Patient Advocate
Listen up! Stem cell scientists craft new ears using children’s own cells
Imagine growing up without an ear, or with one that was stunted and deformed. It would likely have an impact on almost every part of your life, not just your hearing. But now scientists in China say they have found a way to help give children born with this condition a new ear, one that … Continue reading Listen up! Stem cell scientists craft new ears using children’s own cells
The Journey of a Homegrown Stem Cell Research All-Star
Nothing makes a professional sports team prouder than its homegrown talent. Training and mentoring a promising, hard-working athlete who eventually helps carry the team to a championship can lift the spirits of an entire city. Here at CIRM, we hold a similar sense of pride in Brian Fury, one of our own homegrown all-stars. Nearly … Continue reading The Journey of a Homegrown Stem Cell Research All-Star
Alpha clinics and a new framework for accelerating stem cell treatments
Last week, at the World Stem Cell Summit in Miami, CIRM took part in a panel discussion about the role and importance of Alpha Clinics in not just delivering stem cell therapies, but in helping create a new, more collaborative approach to medicine. The Alpha Clinic concept is to create a network of top medical … Continue reading Alpha clinics and a new framework for accelerating stem cell treatments
The Stem Cellar 