It’s hard thinking of something as rare when one in 20 people are at risk of experiencing it in their lifetime. But that’s the situation with rare diseases. There are more than 7,000 of them and each affects under 200,000 people. In some cases they may only affect a few hundred people. But for each … Continue reading Rare Disease Day – fighting for awareness and hope
Month: February 2019
Antibody effective in cure for rare blood disorders
3D illustration of an antibody binding to a designated target. Illustration created by Audra Geras. A variety of diseases can be traced to a simple root cause: problems in the bone marrow. The bone marrow contains specialized stem cells known as hematopoietic stem cells (HSCs) that give rise to different types of blood cells. As … Continue reading Antibody effective in cure for rare blood disorders
Stories that caught our eye: National Geographic takes a deep dive into iPS cells; Japanese researchers start iPS cell clinical trial for spinal cord injury; and do high fat diets increase your risk of colorectal cancer
Can cell therapy beat the most difficult diseases? That’s the question posed in a headline in National Geographic. The answer; maybe, but it is going to take time and money. The article focuses on the use of iPS cells, the man-made equivalent of embryonic stem cells that can be turned into any kind of cell … Continue reading Stories that caught our eye: National Geographic takes a deep dive into iPS cells; Japanese researchers start iPS cell clinical trial for spinal cord injury; and do high fat diets increase your risk of colorectal cancer
CIRM Invests in Chemotherapy-Free Approach to Rare But Deadly Childhood Disease
David Vetter, boy diagnosed with SCID Imagine being told that your seemingly healthy newborn baby has a life-threatening disease. In a moment your whole world is turned upside down. That’s the reality for families with a child diagnosed with severe combined immunodeficiency (SCID). Children with SCID lack a functioning immune system so even a simple … Continue reading CIRM Invests in Chemotherapy-Free Approach to Rare But Deadly Childhood Disease
Major league baseball star and his wife turn to IVF to conceive child free of Huntington’s Disease
Joe Smith, pitcher for the Houston Astros, and his wife, sports reporter Allie LaForce. Smith's family carries the gene for Huntington's Disease. Photo courtesy of Huntington's Disease Society for America website. For many couples, one of the most monumental moments in life is the decision made to conceive a child together and start a family. … Continue reading Major league baseball star and his wife turn to IVF to conceive child free of Huntington’s Disease
A new stem cell derived tool for studying brain diseases
Sergiu Pasca’s three-dimensional culture makes it possible to watch how three different brain-cell types – oligodendrocytes (green), neurons (magenta) and astrocytes (blue) – interact in a dish as they do in a developing human brain. Courtesy of the Pasca lab Neurological diseases are among the most daunting diagnoses for a patient to receive, because they … Continue reading A new stem cell derived tool for studying brain diseases
Breakthrough for type 1 diabetes: scientist discovers how to grow insulin-producing cells
Matthias Hebrok, PhD, senior author of new study that transformed human stem cells into mature, insulin-producing cells. Photo courtesy of UCSF. More often than not, people don't really think about their blood sugar levels before sitting down to enjoy a delicious meal, partake in a tasty dessert, or go out for a bicycle ride. But … Continue reading Breakthrough for type 1 diabetes: scientist discovers how to grow insulin-producing cells
Tips on how to be a great Patient Advocate from three of the best Advocates around
No one sets out to be a Patient Advocate. It’s something that you become because of something that happens to you. Usually it’s because you, or a loved one or a friend, becomes ill and you want to help find a treatment. Whatever the reason, it is the start of a journey that often throws … Continue reading Tips on how to be a great Patient Advocate from three of the best Advocates around
The Stem Cellar 