Researchers at the Sanford Burnham Prebys Medical Discovery Institute (SBP) reported new findings this week that may lead to novel therapeutic strategies for people suffering from Duchenne muscular dystrophy (DMD). DMD, a muscle-wasting disease that affects 1 in 7250 males aged 5 to 24 years in the United States, is caused by a genetic mutation leading … Continue reading Deep dive into muscle repair yields new strategies to combat Duchenne muscular dystrophy
Dystrophin
Using heart stem cells to help boys battling a deadly disorder
It’s hard to imagine how missing just one tiny protein can have such a devastating impact on a person. But with Duchenne Muscular Dystrophy (DMD) the lack of a single protein called dystrophin has deadly consequences. Now a new study is offering hope we may be able to help people with this rare genetic … Continue reading Using heart stem cells to help boys battling a deadly disorder
Stem Cell Stories That Caught Our Eye: Free Patient Advocate Event in San Diego, and new clues on how to fix muscular dystrophy and Huntington’s disease
Stem cell research is advancing so fast that it’s sometimes hard to keep up. That’s one of the reasons we have our Friday roundup, to let you know about some fascinating research that came across our desk during the week that you might otherwise have missed. Of course, another way to keep up with the … Continue reading Stem Cell Stories That Caught Our Eye: Free Patient Advocate Event in San Diego, and new clues on how to fix muscular dystrophy and Huntington’s disease
Family ties help drive UCLA’s search for a stem cell treatment for Duchenne muscular dystrophy
April Pyle, Courtney Young and Melissa Spencer: Photo courtesy UCLA Broad Stem Cell Research Center People get into science for all sorts of different reasons. For Courtney Young the reason was easy; she has a cousin with Duchenne muscular dystrophy. Now her work as part of a team at UCLA has led to a new … Continue reading Family ties help drive UCLA’s search for a stem cell treatment for Duchenne muscular dystrophy
Stem cells could offer hope for deadly childhood muscle wasting disease
Duchenne muscular dystrophy (DMD) is a particularly nasty rare and fatal disease. It predominantly affects boys, slowly robbing them of their ability to control their muscles. By 10 years of age, boys with DMD start to lose the ability to walk; by 12, most need a wheelchair to get around. Eventually they become paralyzed, and … Continue reading Stem cells could offer hope for deadly childhood muscle wasting disease
The Stem Cellar 