Gaurav Shah, M.D., CEO and President of Rocket Pharmaceuticals Leukocyte Adhesion Deficiency-I (LAD-I) is a rare pediatric disease caused by a mutation in a specific gene that causes low levels of a protein called CD18. Due to low levels of CD18, the adhesion of immune cells is affected, which negatively impacts the body’s ability to … Continue reading Positive results from CIRM-funded LAD-I trial presented at the 62nd American Society of Hematology Annual Meeting
American Society of Hematology
Enabling the Best Choice for Patients: The Need for Effective Patient Navigation
Making sure patients get the treatment they need and not a "snake oil" substitute We are at a turning point in regenerative medicine as the first wave of treatments have obtained FDA approval. But at the same time as we see the advance of scientifically rigorous research and regulated products we are also witnessing the … Continue reading Enabling the Best Choice for Patients: The Need for Effective Patient Navigation
CIRM’s Alpha Stem Cell Clinics Given High Profile Role in Clinical Trials Network
Sue and Bill Gross Hall Photo by Hoang Xuan Pham/ UC Irvine There are a growing number of predatory clinics in California and around the US, offering unproven stem cell therapies. For patients seeking a legitimate therapy it can often be hard finding a reliable clinic, one offering treatments based on the rigorous science required … Continue reading CIRM’s Alpha Stem Cell Clinics Given High Profile Role in Clinical Trials Network
An off-the-shelf cancer killer
iPS Cell: Photo from the lab of Kathrin Plath at UCLA One of the hottest areas in cancer research right now is the use of CAR-T treatments. These use the patient’s own re-engineered immune system cells to target and kill the tumor. But the thing that makes it so appealing – using the patient’s own … Continue reading An off-the-shelf cancer killer
Four CIRM Funded Trials Release Results at 2019 ASH Meeting
With more than 17,000 members from nearly 100 countries, the American Society of Hematology (ASH) is an organization composed of clinicians and scientists around the world working to conquer various blood diseases. Currently, they are having their 61st Annual ASH Meeting to highlight some of the exciting work going on in the field. Four of … Continue reading Four CIRM Funded Trials Release Results at 2019 ASH Meeting
World Sickle Cell Day: A View from the Front Line
June 19th is World Sickle Cell Day. Sickle cell disease is an inherited blood disorder that causes normally round red blood cells to take on an abnormal sickle shape, resulting in clogged arteries, severe pain, increased risk of stroke and reduced life expectancy. To mark the occasion we asked Nancy M. Rene to write a … Continue reading World Sickle Cell Day: A View from the Front Line
The Stem Cellar 