THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST It’s hard to think of something as being rare when it affects up to 30 million Americans and 300 million people worldwide. But the truth is there are more than 6,000 conditions – those affecting 200,000 people or fewer – that are considered rare. Today, … Continue reading Joining the movement to fight rare diseases
Month: February 2022
Stem Cell Agency Board Approves Funding for Rare Immune Disorder
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Taylor Lookofsky (center), a person with IPEX syndrome, with his father Brian and Dr. Rosa Bacchetta IPEX syndrome is a rare condition where the body can’t control or restrain an immune response, so the person’s immune cells attack their own healthy tissue. The syndrome mostly affects … Continue reading Stem Cell Agency Board Approves Funding for Rare Immune Disorder
It’s nice to be appreciated
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Photo: courtesy City of Hope No one likes to be taken for granted, to feel that people only like you because you have scads of cash and they want some of it. That’s why it’s so lovely when you feel you are appreciated because of all … Continue reading It’s nice to be appreciated
CIRM CNS Consortium Workshop – Held Feb. 24 & 25, 2022
Note: Post edited to include post-event workshop videos. Watch both workshop videos here and here. THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Shared Stem Cell Laboratory at UCLA Advance World Class Science, Deliver Real World Solutions, Provide Opportunity for All. These comprise the themes of our bold 5-year Strategic Plan. Since its launch … Continue reading CIRM CNS Consortium Workshop – Held Feb. 24 & 25, 2022
CIRM-supported therapy for blood cancers gets FDA fast track
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST People often complain about how long it can take to turn a scientific discovery into an approved therapy for patients. And they’re right. It can take years, decades even. But for Immune-Onc Therapeutics the path to FDA approval may just have been shortened. Back in April … Continue reading CIRM-supported therapy for blood cancers gets FDA fast track
CIRM-Funded Study Helping Babies Battle a Deadly Immune Disorder Gets Boost from FDA
Hataalii Begay, age 4, first child treated with UCSF gene therapy for Artemis-SCID THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST When Hataalii Begay was born in a remote part of the Navajo nation he was diagnosed with a rare, usually fatal condition. Today, thanks to a therapy developed at UCSF and funded by CIRM, … Continue reading CIRM-Funded Study Helping Babies Battle a Deadly Immune Disorder Gets Boost from FDA
How a tiny patch is helping restore lasting vision
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Researchers are working on a stem cell-based retinal implant that could be used for people with with advanced dry age-related macular degeneration. (Photo/ Britney O. Pennington) When Anna Kuehl began losing her vision, she feared losing the ability to read and go on long walks in … Continue reading How a tiny patch is helping restore lasting vision
First Patient Dosed in Phase 1 Clinical Trial for T1D
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST There’s some good news for a company and a therapeutic approach that CIRM has been supporting for many years. In September 2018, CRISPR Theraputics and ViaCyte entered a partnership to discover, develop and market gene-edited stem cell-derived therapies to treat type 1 diabetes (T1D). Today, they may stand … Continue reading First Patient Dosed in Phase 1 Clinical Trial for T1D
Could a common herb help in the fight against COVID-19 and other inflammatory diseases?
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST The culinary herb rosemary is commonly used in our kitchens to season an array of dishes, and is also considered a good source for vitamins and minerals. Rosemary is also valued for its medicinal properties, and has traditionally been used to help alleviate muscle pain, boost the immune and circulatory system, as well as many other health benefits. Now, scientists at Scripps Research have found … Continue reading Could a common herb help in the fight against COVID-19 and other inflammatory diseases?
Meet the man who is unlocking the secrets of autism and sending mini-brains into space
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Dr. Alysson Muotri, UC San Diego Normally if you meet someone who has a mini-fridge filled with brains, your first thought is to call the police. But when that someone is Dr. Alysson Muotri, a professor at U.C. San Diego, your second thought is “do tell … Continue reading Meet the man who is unlocking the secrets of autism and sending mini-brains into space
The Stem Cellar 