CIRM funded study results in the first ever in utero stem cell transplant to treat alpha thalassemia

Imagine being able to cure a genetic disorder before a baby is even born. Thanks to a CIRM funded study, what would have been a mere dream a couple of years ago has become a reality. Drs. Tippi MacKenzie and Juan Gonzalez Velez of the University of California San Francisco (UCSF) have successfully treated alpha … Continue reading CIRM funded study results in the first ever in utero stem cell transplant to treat alpha thalassemia