The California Institute for Regenerative Medicine (CIRM) awarded $5,444,353 to Dr. Natalia Gomez-Ospina and her team at Stanford University for a late-stage preclinical program targeting Severe Mucopolysaccharidosis type 1, also known as Hurler syndrome. This inherited condition is caused by a faulty gene. Children with Hurler syndrome lack an enzyme that the body needs to digest sugar. … Continue reading Investing in a stem cell treatment for Hurler syndrome
Hurler syndrome
Making kidney transplants easier for kids and charting a new approach to fighting solid tumors.
Every year, California performs around 100 kidney transplants in children, but, on average, around 50 of these patients will have their bodies reject the transplant. Improving kidney transplant outcomes These children then have to undergo regular dialysis while waiting for a new organ. Even the successful transplants require a lifetime of immunosuppression medications. These medications … Continue reading Making kidney transplants easier for kids and charting a new approach to fighting solid tumors.