THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Caleb Sizemore, photo by Todd Dubnicoff Caleb Sizemore says growing up with Duchenne’s Muscular Dystrophy (DMD) was tough. The disease is a rare genetic disorder that slowly destroys a person’s muscles, impairing their ability to walk or breathe. Eventually it attacks the heart leading to premature … Continue reading HOPE for patients with a muscle destroying disease
Caleb Sizemore
Two rare diseases, two pieces of good news
Dr. Stephanie Cherqui Last week saw a flurry of really encouraging reports from projects that CIRM has supported. We blogged about two of them last Wednesday, but here’s another two programs showing promising results. UC San Diego researcher Dr. Stephanie Cherqui is running a CIRM-funded clinical trial for cystinosis. This is a condition where patients … Continue reading Two rare diseases, two pieces of good news
New CIRM Alpha Stem Cell Clinic offers HOPE for boys with deadly disease
For people battling Duchenne Muscular Dystrophy (DMD), a rare and fatal genetic disorder that slowly destroys muscles, hope has often been in short supply. There is no cure and treatments are limited. But now a new clinical trial at the site of one of the newest CIRM Alpha Stem Cell Clinic Network members could change … Continue reading New CIRM Alpha Stem Cell Clinic offers HOPE for boys with deadly disease
Using heart stem cells to help boys battling a deadly disorder
It’s hard to imagine how missing just one tiny protein can have such a devastating impact on a person. But with Duchenne Muscular Dystrophy (DMD) the lack of a single protein called dystrophin has deadly consequences. Now a new study is offering hope we may be able to help people with this rare genetic … Continue reading Using heart stem cells to help boys battling a deadly disorder
Family, faith and funding from CIRM inspire one patient to plan for his future
Having been to many conferences and meetings over the years I have found there is a really simple way to gauge if someone is a good speaker, if they have the attention of people in the room. You just look around and see how many people are on their phones or laptops, checking their email … Continue reading Family, faith and funding from CIRM inspire one patient to plan for his future
The Stem Cellar 