Despite advances in treatments in recent years heart disease remains the leading cause of death in the US. It accounts for one in three deaths in this country, and many people are not even aware they have a problem until they have a heart attack. One of the early warning signs of danger is a … Continue reading Using stem cells and smart machines to warn of heart problems
Research News
A big deal for type 1 diabetes
It’s not often you get excited talking about company mergers, but a deal announced today is something worth getting excited about, particularly if you have type 1 diabetes (T1D). Today Vertex announced it was buying ViaCyte for $320 million in cash. Why is that important? Because both companies are working on developing stem cell therapies … Continue reading A big deal for type 1 diabetes
First patient dosed in clinical trial for a drug-resistant form of epilepsy
Tablet BM47753. Neo-Babylonian Period. Courtesy of the British Museum, London. Epilepsy seems to have been a problem for people for as long as people have been around. The first recorded mention of it is on a 4000-year-old Akkadian tablet found in Mesopotamia (modern day Iraq). The tablet includes a description of a person with "his … Continue reading First patient dosed in clinical trial for a drug-resistant form of epilepsy
Creating a ‘bespoke’ approach to rare diseases
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Up until recently the word “bespoke” meant just one thing to me, a hand-made suit, customized and fitted to you. There’s a street in London, Saville Row, that specializes in these suits. They’re gorgeous. They’re also very expensive and so I thought I’d never have a … Continue reading Creating a ‘bespoke’ approach to rare diseases
The long road to developing a therapy for epilepsy
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Good science takes time. That’s an important guiding phrase for researchers looking to develop new therapies. But it’s also a frustrating reality for patients who are waiting for something to help them now. That point was driven home last week when the governing board of the … Continue reading The long road to developing a therapy for epilepsy
The power of the patient advocate: how a quick visit led to an $11M grant to fund a clinical trial
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Members of NFOSD visiting UC Davis in 2013 At the California Institute for Regenerative Medicine (CIRM) we are fortunate in having enough money to fund the most promising research to be tested in a clinical trial. Those are expensive projects, often costing tens of millions of … Continue reading The power of the patient advocate: how a quick visit led to an $11M grant to fund a clinical trial
It’s hard to be modest when people keep telling you how good you are
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST I have a confession. Deep down I’m shallow. So when something I am part of is acknowledged as one of the best, I delight in it (my fellow bloggers Katie and Esteban also delight in it, I am just more shameless about letting everyone know.) And … Continue reading It’s hard to be modest when people keep telling you how good you are
Chance discovery could lead to a treatment for skin ulcers
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Dr. Antoni Ribas in his research lab on the UCLA Campus: Photo courtesy Ann Johansson When UCLA's Dr. Antoni Ribas was researching a potential therapy for melanoma, a form of skin cancer, he stumbled upon something unexpected. That unexpected discovery has now resulted in him getting … Continue reading Chance discovery could lead to a treatment for skin ulcers
Stem Cell Agency Board Approves Funding for Rare Immune Disorder
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Taylor Lookofsky (center), a person with IPEX syndrome, with his father Brian and Dr. Rosa Bacchetta IPEX syndrome is a rare condition where the body can’t control or restrain an immune response, so the person’s immune cells attack their own healthy tissue. The syndrome mostly affects … Continue reading Stem Cell Agency Board Approves Funding for Rare Immune Disorder
It’s nice to be appreciated
THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Photo: courtesy City of Hope No one likes to be taken for granted, to feel that people only like you because you have scads of cash and they want some of it. That’s why it’s so lovely when you feel you are appreciated because of all … Continue reading It’s nice to be appreciated