CIRM-supported therapy for blood cancers gets FDA fast track

THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST People often complain about how long it can take to turn a scientific discovery into an approved therapy for patients. And they’re right. It can take years, decades even. But for Immune-Onc Therapeutics the path to FDA approval may just have been shortened. Back in April … Continue reading CIRM-supported therapy for blood cancers gets FDA fast track

CIRM-Funded Study Helping Babies Battle a Deadly Immune Disorder Gets Boost from FDA

Hataalii Begay, age 4, first child treated with UCSF gene therapy for Artemis-SCID THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST When Hataalii Begay was born in a remote part of the Navajo nation he was diagnosed with a rare, usually fatal condition. Today, thanks to a therapy developed at UCSF and funded by CIRM, … Continue reading CIRM-Funded Study Helping Babies Battle a Deadly Immune Disorder Gets Boost from FDA

How a tiny patch is helping restore lasting vision

THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Researchers are working on a stem cell-based retinal implant that could be used for people with with advanced dry age-related macular degeneration. (Photo/ Britney O. Pennington) When Anna Kuehl began losing her vision, she feared losing the ability to read and go on long walks in … Continue reading How a tiny patch is helping restore lasting vision

First Patient Dosed in Phase 1 Clinical Trial for T1D

THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST There’s some good news for a company and a therapeutic approach that CIRM has been supporting for many years. In September 2018, CRISPR Theraputics and ViaCyte entered a partnership to discover, develop and market gene-edited stem cell-derived therapies to treat type 1 diabetes (T1D). Today, they may stand … Continue reading First Patient Dosed in Phase 1 Clinical Trial for T1D

Meet the man who is unlocking the secrets of autism and sending mini-brains into space

THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Dr. Alysson Muotri, UC San Diego Normally if you meet someone who has a mini-fridge filled with brains, your first thought is to call the police. But when that someone is Dr. Alysson Muotri, a professor at U.C. San Diego, your second thought is “do tell … Continue reading Meet the man who is unlocking the secrets of autism and sending mini-brains into space

CIRM Board gives thumbs up to training and treatment programs

THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST CIRM Bridges student discusses her poster presentation At CIRM, the bread and butter of what we do is funding research and hopefully advancing therapies to patients. But the jam, that's our education programs. Helping train the next generation of stem cell and gene therapy scientists is … Continue reading CIRM Board gives thumbs up to training and treatment programs

Making stem cell and gene therapies available and affordable for all California patients

THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST Developing a new therapy: Photo courtesy UCLA There is no benefit in helping create a miraculous new therapy that can cure people and save lives if no one except the super-rich can afford it. That’s why the California Institute for Regenerative Medicine (CIRM) has made creating … Continue reading Making stem cell and gene therapies available and affordable for all California patients

Breaking down barriers: Expanding patient access and accelerating research

THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST 10 years ago I was presented with an incredibly unique opportunity- to become the fifth patient with spinal cord injuries to participate in the world's first clinical trial testing a treatment made from human embryonic stem cells. It was not only a risky and potentially life-changing decision, … Continue reading Breaking down barriers: Expanding patient access and accelerating research

Overcoming obstacles and advancing treatments to patients

THIS BLOG IS ALSO AVAILABLE AS AN AUDIO CAST UC Davis GMP Manufacturing facility: Photo courtesy UC Davis When you are trying to do something that has never been done before, there are bound to be challenges to meet and obstacles to overcome. At the California Institute for Regenerative Medicine (CIRM) we are used to … Continue reading Overcoming obstacles and advancing treatments to patients

CIRM-funded stem cell clinical trial patients: Where are they now?

Ronnie with his parents Pawash Priyank and Upasana Thakur. Since its launch in 2004, the California Institute for Regenerative Medicine (CIRM) has been a leader in growing the stem cell and regenerative medicine field while keeping the needs of patients at the core of its mission.  To date, CIRM has:   Advanced stem cell research and therapy development for … Continue reading CIRM-funded stem cell clinical trial patients: Where are they now?