Image source: SickKids -Terry, Georgia, and Michael Pirovolakis CIRM awarded Elpida Therapeutics a $3.9 million grant in December 2023 to support a pioneering preclinical study on Charcot Marie Tooth disease type 4J (CMT4J). CMT4J is an ultra-rare, inherited condition that primarily affects the nerves outside the brain and spinal cord. It accounts for about 0.24% … Continue reading Story of Hope: Elpida Therapeutics’ Pioneer Study on Rare Nerve Disease CMT4J
Access and Affordability
CIRM approves $2.5 million to establish a Patient Support Program
Hataalii Tiisyatonii Begay (HT) participated in a CIRM-funded clinical trial at UCSF for Artemis-SCID, a condition that can be life-threatening or fatal. Photo courtesy Barbara Ries / UCSF. The California Institute for Regenerative Medicine (CIRM) funds innovative cell and gene therapy research and educational programs to advance regenerative medicine in the Golden State. Just as … Continue reading CIRM approves $2.5 million to establish a Patient Support Program
Finding solutions for affordable and accessible cell and gene therapies
The California Institute for Regenerative Medicine (CIRM) is not alone in seeking a way to make cell and gene therapies more affordable and accessible. The Innovative Genomics Institute (IGI) just completed a year-long effort to consider how treatments could be made more accessible. This effort involved creating a task force comprised of 30 participants to … Continue reading Finding solutions for affordable and accessible cell and gene therapies
The Stem Cellar 