Image Source: American Heart Association Journals The California Institute for Regenerative Medicine (CIRM) recently awarded $4 million to support the development of a one-time gene therapy for desmoplakin gene variant arrhythmogenic cardiomyopathy (DSP ACM), a rare and life-threatening genetic disorder. This preclinical award to Deborah D. Ascheim, MD, and her team at Rejuvenate Bio are … Continue reading CIRM $4 million awarded to support innovative Gene Therapy for Rare Heart Disorder
Genetic disorder
Gene-editing Technique in Mice Shows Promise for Genetic Disorder in Utero
For first time ever, scientists used a gene editing technique to successfully cure a genetic condition in a mouse in utero. Their findings present a promising new avenue for research into treating genetic conditions in utero.
The Stem Cellar 