From left to right: Brian Lookofsky, Taylor Lookofsky, and Rosa Bacchetta, M.D. Picture taken in October 2019 Last year, CIRM awarded $5.53 million to Rosa Bacchetta, M.D. at Stanford University to complete the work necessary to conduct a clinical trial for IPEX syndrome, a rare pediatric disease. This rare disease is caused by mutations in the FOXP3 gene, … Continue reading CIRM-funded treatment gets orphan drug and rare pediatric disease designations from FDA
FOXP3
Stem Cell Agency Approves Funding for Clinical Trials Targeting Parkinson’s Disease and Blindness
The governing Board of the California Institute for Regenerative Medicine (CIRM) yesterday invested $32.92 million to fund the Stem Cell Agency’s first clinical trial in Parkinson’s disease (PD), and to support three clinical trials targeting different forms of vision loss. This brings the total number of clinical trials funded by CIRM to 60. The PD … Continue reading Stem Cell Agency Approves Funding for Clinical Trials Targeting Parkinson’s Disease and Blindness