CIRM-Funded Study of Deadly Immune Disorder Gets Boost from FDA

Hataalii Begay, age 4, first child treated with UCSF gene therapy for Artemis-SCID When Hataalii Begay was born in a remote part of the Navajo nation he was diagnosed with a rare, usually fatal condition, Artemis-SCID. New stem cell therapy Today, thanks to a therapy developed at UCSF and funded by CIRM, he's a normal healthy … Continue reading CIRM-Funded Study of Deadly Immune Disorder Gets Boost from FDA

Celebrating Ja’Ceon Golden

Meet Ja’Ceon Golden. He was among the first patients treated at UC San Francisco, in partnership with St. Jude Children’s Research Hospital, in a CIRM-funded study for Severe Combined Immunodeficiency. Ja’Ceon was born without a functioning immune system, so even a simple cold could have been fatal. At UCSF, Dr. Mort Cowan’s team collected Ja’Ceon’s … Continue reading Celebrating Ja’Ceon Golden

Living proof science can find a cure

Like many kids, let’s face it, many adults too, Ronav “Ronnie” Kashyap is getting a little bored stuck inside all day during the coronavirus pandemic. This video, shot by his dad Pawash, shows Ronnie trying to amuse himself by pretending to be hard at work. https://www.instagram.com/p/B_BSQaonFXb/ It’s a lovely moment. It’s also a moment that … Continue reading Living proof science can find a cure

CIRM-funded therapy helps “bubble babies” lead a normal life

Ja'Ceon Golden; 'cured" of SCID At CIRM we are very cautious about using the “c” word. Saying someone has been “cured” is a powerful statement but one that loses its meaning when over used or used inappropriately. However, in the case of a new study from U.C. San Francisco and St. Jude Children’s Research Hospital … Continue reading CIRM-funded therapy helps “bubble babies” lead a normal life