Dr. Stephanie Cherqui The future looks brighter for cystinosis patients and their families. As one of 7,000 rare diseases, cystinosis causes an abnormal build-up of the amino acid cystine that can lead to organ failure and premature death. With little to no treatment options, children and young adults primarily affected by the condition often have … Continue reading Novartis acquisition validates CIRM’s impact on cystinosis treatment
Month: June 2023
CIRM invests $10 million to build California Cell and Gene Therapy Manufacturing Network
A laboratory at UCLA's current good manufacturing practices facility | Photo credit: Elena Zhukova The California Institute for Regenerative Medicine (CIRM), the world’s largest institution dedicated to regenerative medicine, awarded $10 million to five facilities as part of the first phase to build a California Cell and Gene Therapy Manufacturing Network. The awards include: Application … Continue reading CIRM invests $10 million to build California Cell and Gene Therapy Manufacturing Network
The Stem Cellar 