If you are born with Severe Combined Immunodeficiency (SCID), your childhood is anything but normal. You don’t get to play with other kids, or be held by your parents. You can’t even breathe the same air. And, without treatment, you probably won’t live past your first year. This is the reality of SCID, also called … Continue reading Gene Therapy Beats Half-Matched Stem Cell Transplant in Side-by-Side Comparison to Treat ‘Bubble Baby’ Disease
bubble baby disease
Potential treatment for sickle cell disease close
Scientists at UCLA found a potentially treatment for sickle cell disease, a new method of gene therapy that can correct the genetic mutation and help the body on its way to generate normal, healthy blood cells for the rest of the patient’s life. The study, funded in part by CIRM and reported in the journal … Continue reading Potential treatment for sickle cell disease close