Image Credit: The Adler Lab at the University of California, San Diego In the fall of 2024, the California Institute for Regenerative Medicine (CIRM) helped sponsor the Gene Therapy Initiative symposium in La Jolla, CA. While there, CIRM staff caught up with a few CIRM grantees who are working on gene therapy approaches to treating … Continue reading Gene Therapy for Heart Failure: A Conversation with Eric Adler, MD
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Gene therapies for Friedreich’s Ataxia: A conversation with Liz Soragni, PhD
Liz Soragni, PhD, Director of Research at the Friedreich’s Ataxia Research Alliance In the fall of 2024, the California Institute for Regenerative Medicine (CIRM) helped sponsor the Gene Therapy Initiative symposium in La Jolla, CA. While there, CIRM staff caught up with a few CIRM grantees who are working on gene therapy approaches to treating … Continue reading Gene therapies for Friedreich’s Ataxia: A conversation with Liz Soragni, PhD
The Stem Cellar’s Most Read Blogs of 2024
2024 was a significant year for the California Institute for Regenerative Medicine (CIRM). We reached major milestones, celebrated our 20th anniversary, and introduced our Strategic Allocation Framework (SAF) impact goals. We did this all while continuing to fund innovative work in regenerative medicine. The Stem Cellar blog is where we share these stories, providing readers … Continue reading The Stem Cellar’s Most Read Blogs of 2024
Potential Gene Therapy for Children with ADA-SCID
Photo Courtesy of Andrea Fernandez de Soto Imagine stepping outside and facing life‑threatening danger. For children born with ADA‑SCID (adenosine deaminase severe combined immunodeficiency), this is daily life. Their immune systems are so weak that a cold or a scraped knee can cause a dangerous infection. Donald Kohn, MD, a leading researcher at the UCLA … Continue reading Potential Gene Therapy for Children with ADA-SCID
Celebrating Two Decades of Progress with CIRM’s 2024 Annual Report
Celebrate with us our two decades of progress. Our 2024 Annual Report highlights 20 years of advancing regenerative medicine. For twenty years, CIRM has pushed the boundaries of stem cell and gene therapy. We have funded more than 109 clinical trials and built the infrastructure that drives research and development. Our work has fueled innovation, … Continue reading Celebrating Two Decades of Progress with CIRM’s 2024 Annual Report
Elpida Therapeutics’ Study on Rare Nerve Disease CMT4J
CIRM awarded Elpida Therapeutics a $3.9 million grant in December 2023 to support a pioneering preclinical study on Charcot Marie Tooth disease type 4J (CMT4J).
Solano Student’s Life-Saving Bone Marrow Match Begins with One Swab
Image Source: Jose Solorio Jose Solorio, a Solano Community College student and participant in CIRM’s COMPASS training program, has firsthand experience in witnessing the power of stem cells as a donor after he became a bone marrow match. Hands-on research As part of CIRM's COMPASS program, which provides hands‑on research experience across 16 programs statewide … Continue reading Solano Student’s Life-Saving Bone Marrow Match Begins with One Swab
A Conversation with CEO Cory Nicholas on Neurona Therapeutics’ Recent RMAT Designation
At the California Institute for Regenerative Medicine (CIRM), we highlight achievements from the research we support. We recently spoke with Cory Nicholas, PhD, CEO and Co‑Founder of Neurona Therapeutics, about a major milestone for the clinical‑stage company. Neurona received the FDA’s Regenerative Medicine Advanced Therapy (RMAT) designation for NRTX‑1001, a CIRM‑funded neural cell therapy for … Continue reading A Conversation with CEO Cory Nicholas on Neurona Therapeutics’ Recent RMAT Designation
A CIRM Bridges Trainee’s Path into Regenerative Medicine
Josh Nelson, a former technical director for various theaters, tapped into CIRM's Bridges program at Cal Poly Humbolt to establish a career in regenerative medicine research.
Finding affordable cell and gene therapies
The California Institute for Regenerative Medicine (CIRM) is not alone in looking for ways to make cell and gene therapies more affordable and accessible. The Innovative Genomics Institute (IGI) recently completed a year‑long effort to explore how to expand access to these treatments. IGI formed a task force of 30 experts to develop options. The … Continue reading Finding affordable cell and gene therapies